Loading...
Dernières publications
-
Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
-
A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
-
Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Human Umbilical Vein Endothelial Cells
Molecular docking
Dystrophin-EGFP
Long QT
Becker muscular dystrophy BMD
Skeletal muscle
Male
LKB1
Autophagy
Inhibitors
Dystrophin central domain
NNOS
Cell homeostasis
Molecular Sequence Data
NAD+
Homeostasis
Dynamin 2
Becker BMD muscular dystrophy
Drp1
DMD
Long noncoding RNA
Cardiomyopathy
Knockout
Dystrophin
DMO
Antisense oligonucleotides
Muscle development
Animal/physiopathology
DHPR α1S
Duchenne muscular dystrophy
L-Type
Morphogenesis
Muscles/physiopathology
CD38
BMD
Muscle
Muscle Biology
Multiresolution modeling
Myogenesis
Allele‐specific silencing therapy
Invivo
Animals
Multi exon skipping
Hepatocellular carcinoma
Dystrophine
Mdx mouse
Dystrophie Musculaire de Duchenne DMD
Inbred C57BL
Delivery
Gene Expression Regulation/drug effects
Cachexia
Myotendinous junction
Muscle Strength
Gene expression
Genomic
MES
Muscular Dystrophy
Gene modifiers
Immunoglobulin Fc Fragments/pharmacology
Liver
CaVβs
Muscular Atrophy
Activin Receptors
CaV subunits
Exon skipping
Clinical trials
Ex-vivo
Dystrophie Musculaire de Becker BMD
Epigenetics
CTNNB1
Centronuclear myopathy
Dystrophie musculaire de Becker
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Duchenne DMD dystrophy
Cell Line
Base Sequence
Modificateurs de gènes
Calcium
Diseases
LncARN
Becker muscular dystrophy
Inbred mdx
MiARN
Calcium Channels
Mice
Dystrophy
Metabolism
Cell Biology
Humans
Multi resolution modeling
LncRNA
Génomique
Duchenne muscular dystrophy DMD
Cultured
Hear
Cardiomyopathie
Mitochondrial fission
Cells
Energy Metabolism/drug effects
Muscular dystrophy